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  • Thursday, Nov 2nd
    8:30 AM – 9:10 AM MST
    RFPT01--Technologies to Achieve Efficient & Durable CFTR Rescue
    Location: Theater A (Exhibit & Poster Hall)
    Chair: Anthony J. Fischer, MD, PhD (he/him/his) – Stead Family Department of Pediatrics
    Chair: Silvia M. Kreda, n/a (she/her/hers) – University of North Carolina
    PTAC/CFTR
  • Thursday, Nov 2nd
    9:30 AM – 11:00 AM MST
    TPS01--Stem Cell Biology, Reprogramming, and Engraftment in CF Lungs
    Location: Theater C (Exhibit & Poster Hall)
    Chair: Amy L. Ryan, PhD – University of Iowa
    Chair: Finn Hawkins, MB BCh – Boston University Medical Center
    PTAC/CFTR
  • Thursday, Nov 2nd
    9:45 AM – 11:45 AM MST
    W05--Rescuing CFTR Premature Truncation Alleles: Basic Biology & Novel Therapeutic Strategies
    Location: 105 C (West)
    Chair: John D. Lueck – University of Rochester School of Medicine and Dentistry
    Chair: Jianguo Chen, MD – Cystic Fibrosis Research Center, University of Alabama at Birmingham.
    PTAC/CFTR
  • Thursday, Nov 2nd
    12:00 PM – 1:30 PM MST
    LL02--Cellular Barriers to Nucleotide-Based (PTAC-Type) Interventions
    Location: 228 AB (North)
    Chair: Kara Foshay, PhD (she/her/hers) – Cystic Fibrosis Foundation
    Chair: Patrick T. Harrison, PhD – University College Cork
    Speaker: Kara Foshay, PhD (she/her/hers) – Cystic Fibrosis Foundation
    Speaker: Patrick T. Harrison, PhD – University College Cork
    PTAC/CFTR
  • Thursday, Nov 2nd
    12:00 PM – 1:30 PM MST
    RT28- Environmental Factors that Influence CFTR Biogenesis, Expression, and Activity
    Location: 229 AB (North)
    Facilitator: Estelle A. Cormet-Boyaka, PhD (she/her/hers) – The Ohio State University
    PTAC/CFTRAPPTTIMI
  • Thursday, Nov 2nd
    12:00 PM – 1:30 PM MST
    RT29- Proteomic-driven advances in studies of CF
    Location: 229 AB (North)
    Facilitator: Lars Plate, PhD (he/him/his) – Vanderbilt University
    PTAC/CFTRAPPTT
  • Thursday, Nov 2nd
    12:00 PM – 1:30 PM MST
    RT30- Emerging viral and non-viral delivery vehicles for genetic rescue of airway epithelium
    Location: 229 AB (North)
    Facilitator: Hugh Smyth, PhD (he/him/his) – The University of Texas at Austin
    PTAC/CFTR
  • Thursday, Nov 2nd
    12:00 PM – 1:30 PM MST
    RT31- Techniques to detect CFTR function in cells and tissues
    Location: 229 AB (North)
    Facilitator: S. Vamsee Raju, BPharm, PhD – University of Alabama at Birmingham
    PTAC/CFTR
  • Thursday, Nov 2nd
    2:00 PM – 4:00 PM MST
    S11--Nucleotide Delivery to CF Lungs: Emerging Strategies and Barriers to Success
    Location: 102 AB (West)
    Chair: Alexandra S. Piotrowski-Daspit, PhD (she/her/hers) – University of Michigan
    Chair: Patrick Sinn, PhD (he/him/his) – University of Iowa
    PTAC/CFTRAPPTT
  • Friday, Nov 3rd
    9:30 AM – 11:30 AM MST
    W29--Accelerating Progress Along the Path to a Cure
    Location: 212 A-C (West)
    Chair: Ashley Cooney, PhD – University of Iowa
    PTAC/CFTR
  • Friday, Nov 3rd
    3:30 PM – 5:30 PM MST
    S14--Restoration of CFTR Ion Transport for All People With CF
    Location: 102 AB (West)
    Chair: Deepika Polineni, MD, MPH (she/her/hers) – Washington University School of Medicine in St. Louis
    Chair: Paul B. McCray, Jr., MD (he/him/his) – University of Iowa
    PTAC/CFTR
  • Friday, Nov 3rd
    3:30 PM – 5:30 PM MST
    S17--CFTR Structure, Function, & Cellular Biology
    Location: 103 AB (West)
    Chair: Gergely L. Lukacs, MD, PhD – McGill University
    Chair: Ines Pankonien, n/a (she/her/hers) – BioISI – Biosystems & Integrative Sciences Institute, Faculty of Sciences, University of Lisboa, Lisboa Portugal
    PTAC/CFTR
  • Saturday, Nov 4th
    7:15 AM – 9:15 AM MST
    W31--Fundamental Discoveries to Elucidate CFTR Cell Biology & Ion Transport
    Location: 105 C (West)
    Chair: Kathryn E. Oliver, PhD (she/her/hers) – Emory University School of Medicine
    Chair: John W. Hanrahan, PhD (he/him/his) – McGill University
    PTAC/CFTR
  • Saturday, Nov 4th
    9:30 AM – 11:30 AM MST
    S25--Genetic Repair of CFTR: Advancement of Superexon, Editing, & Related Technologies
    Location: 103 AB (West)
    Chair: Hillary Valley, PhD (she/her/hers) – Cystic Fibrosis Foundation
    Chair: Brian R. Davis, PhD – Univ. Alabama at Birmingham Cystic Fibrosis Research Center
    PTAC/CFTR
  • Saturday, Nov 4th
    11:45 AM – 1:15 PM MST
    LL10--What are the Most Relevant Clinical Outcomes in PTAC-Based Trials
    Location: 225 AB (North)
    Chair: Marie E. Egan, MD – Yale University School of Medicine
    Chair: Claire Keating, MD – Columbia University Irving Medical Center
    Speaker: George M. Solomon, MD – University of Alabama at Birmingham, Birmingham, AL USA
    Speaker: Felix Ratjen, MD, PhD, FRCPC, FERS – University of Toronto, Hospital for Sick Children
    PTAC/CFTRAPPTT
  • Saturday, Nov 4th
    11:45 AM – 1:15 PM MST
    RT49- Climate Change & Impact on Patients with CF
    Location: 224 AB (North)
    Facilitator: Jonathan Cogen, MD, MPH (he/him/his) – Seattle Children's Hospital/University of Washington
    Facilitator: Alan Genatossio, Seattle, USA – Seattle Children's Hospital
    PTAC/CFTRAPPTT
  • Saturday, Nov 4th
    11:45 AM – 1:15 PM MST
    RT50- Reagents to detect CFTR expression for monitoring CFTR in cells and tissues
    Location: 224 AB (North)
    Facilitator: Martina Gentzsch, PhD (she/her/hers) – University of North Carolina
    PTAC/CFTR
  • Saturday, Nov 4th
    11:45 AM – 1:15 PM MST
    RT51- Omics and relevance to cystic fibrosis basic science and therapeutic outcomes
    Location: 224 AB (North)
    Facilitator: Bruce Stanton, PhD – Geisel School of Medicine at Dartmouth
    PTAC/CFTR
  • Saturday, Nov 4th
    11:45 AM – 1:15 PM MST
    RT52- DNA editing-based approaches to optimizing rescue of CFTR
    Location: 224 AB (North)
    Facilitator: Shingo Suzuki, PhD – University of Alabama at Birmingham
    PTAC/CFTR